Ohioans are curing debilitating pediatric diseases, creating less invasive surgical tools, programming highly accurate diagnostic imaging techniques, improving provider processes to reduce patient costs, personalizing medication delivery for individual patients, and much more.
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The film The Weight of a Mountain is about the children and families who are struggling to deal with the devastating effects of Sanfilippo Syndrome. It is also about the father of two Sanfilippo children and the CEO of Abeona Therapeutics who chose to climb a mountain to raise awareness of the disease and bring in needed funding for research.
When Evie was born, she wasn’t expected to survive due to the rare metabolic bone disease hypophosphotasia (HPP), which affects bone growth, breathing, and mobility. At the time of her birth, there was no treatment. Charles River works with the world’s leading pharmaceutical companies by providing expertise along the entire drug discovery and development continuum.
Three-year-old Brayden Newbold’s parents brought him to Cincinnati Children’s for treatment when they noticed he wasn’t growing as expected. He was diagnosed with Laron syndrome, a growth disorder that causes small stature. Due to treatment at Cincinnati Children’s, Brayden Newbold has grown 3 1/2 inches since taking Increlex injections over the last 9 months. Brayden continues receiving treatment at Cincinnati Children’s Growth Center in the division of Endocrinology.
It is estimated that a third of the almost 800,000 Americans with cerebral palsy have hemiplegia, which results in disuse of the weaker hand in everyday life from childhood on with very few effective treatments. Contralaterally Controlled Functional Electrical Stimulation (CCFES) will assess a new therapy from the Cleveland FES Center for improving hand function in children with hemiplegic cerebral palsy.
While Lauren battles acute lymphoblastic leukemia and faces some tough side effects from her treatment, she inspires kids everywhere with her determination and spunk. Nationwide Children’s is determined to make a difference for kids like Lauren. Doctors and researchers work together to create significant advances in treatments for childhood cancer to help kids everywhere.
Limb-girdle muscular dystrophy (LGMD) is a group of monogenic diseases that cause weakness and wasting of the muscles in the arms and legs. Plavi Mittal, Brad Williams and others describe what LGMD2B/MM is, who it affects, and the importance of a cure no matter what stage of disease progression a person is experiencing. Myonexus Therapeutics is developing first ever treatments for the disease.
Uplifting Videos from Ohio’s Hospitals
Even on the days when a patient gets a depressing diagnosis or things seem to be going wrong, people at Cincinnati Children’s have a way of believing in the power of a smile to help make things OK. This is what happened when doctors, nurses, patients and staff from Cincinnati Children’s got together to put our own spin on rapper Flo Rida’s hit “Good Feeling.”
Patients, doctors, nurses and staff at UH Rainbow Babies & Children’s Hospital got into the lip sync phenomena, singing and dancing to One Direction’s “What Makes You Beautiful” as part of the new #ThisIsRainbow campaign.